A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice

Haiyan Zhou, Narinder Janghra, Chalermchai Mitrpant, Rachel L. Dickinson, Karen Anthony, Loren Price, Ian C. Eperon, Stephen D. Wilton, Jennifer Morgan, Francesco Muntoni

Research output: Contribution to JournalArticlepeer-review

Fingerprint

Dive into the research topics of 'A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice'. Together they form a unique fingerprint.

Medicine & Life Sciences