A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice

  • Haiyan Zhou
  • , Narinder Janghra
  • , Chalermchai Mitrpant
  • , Rachel L. Dickinson
  • , Karen Anthony
  • , Loren Price
  • , Ian C. Eperon
  • , Stephen D. Wilton
  • , Jennifer Morgan
  • , Francesco Muntoni

Research output: Contribution to Journal › Article › peer-review

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Keyphrases

Biochemistry, Genetics and Molecular Biology

Medicine and Dentistry

Neuroscience