Biochemical and clinical variability of Becker muscular dystrophy: Predicting optimal target exons for exon skipping therapy in Duchenne muscular

Karen Anthony, Virginia Arechavala-Gomeza, Valeria Ricotti, Silvia Torelli, Lucy Feng, Giorgio Tasca, Michela Guglieri, Rita Barresi, Annarita Armaroli, Alessandra Ferlini, Kate Bushby, Volker Straub, Enzo Ricci, Caroline Sewry, Jennifer Morgan, Francesco Muntoni

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Medicine & Life Sciences