Dystrophin quantification and clinical correlations in Becker muscular dystrophy: Implications for clinical trials

Karen Anthony, Sebahattin Cirak, Silvia Torelli, Giorgio Tasca, Lucy Feng, Virginia Arechavala-Gomeza, Annarita Armaroli, Michela Guglieri, Chiara S. Straathof, Jan J. Verschuuren, Annemieke Aartsma-Rus, Paula Helderman-Van Den Enden, Katherine Bushby, Volker Straub, Caroline Sewry, Alessandra Ferlini, Enzo Ricci, Jennifer E. Morgan, Francesco Muntoni

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Medicine & Life Sciences