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Dystrophin quantification and clinical correlations in Becker muscular dystrophy: Implications for clinical trials

  • Karen Anthony
  • , Sebahattin Cirak
  • , Silvia Torelli
  • , Giorgio Tasca
  • , Lucy Feng
  • , Virginia Arechavala-Gomeza
  • , Annarita Armaroli
  • , Michela Guglieri
  • , Chiara S. Straathof
  • , Jan J. Verschuuren
  • , Annemieke Aartsma-Rus
  • , Paula Helderman-Van Den Enden
  • , Katherine Bushby
  • , Volker Straub
  • , Caroline Sewry
  • , Alessandra Ferlini
  • , Enzo Ricci
  • , Jennifer E. Morgan
  • , Francesco Muntoni

Research output: Contribution to Journal › Article › peer-review

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