Exon Skipping Quantification by Quantitative Reverse-Transcription Polymerase Chain Reaction in Duchenne Muscular Dystrophy Patients Treated with the Antisense Oligomer Eteplirsen

Karen Anthony, Lucy Feng, Virginia Arechavala-Gomeza, Michela Guglieri, Volker Straub, Katherine Bushby, Sebahattin Cirak, Jennifer Morgan, Francesco Muntoni

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