Restoration of the dystrophin-associated glycoprotein complex after exon skipping therapy in duchenne muscular dystrophy

Sebahattin Cirak
, Lucy Feng
, Karen Anthony
, Virginia Arechavala-Gomeza
, Silvia Torelli
, Caroline Sewry
, Jennifer E. Morgan
, Francesco Muntoni

Research output: Contribution to Journal › Article › peer-review

1 results
- Title(descending)

FDA approves first drug to treat Duchenne muscular dystrophy (DMD)
Anthony, K. (Co-Investigator)
Impact: Public policy impacts, Health and Well-Being impacts, Quality of life impacts, 03: Good Health and Well-Being (UN SDG)